With early detection, a child with Duchenne’s Muscular Dystrophy (DMD), can get treatment to slow the progress of the disease. This means that your child or young person may stay mobile longer and live more independently and longer than they would without specialized care and management.
Parents and caregivers can
Slowing disease progression
and quality of life
Prescription drugs that help slow the loss of muscle function and treat the symptoms of DMD.
Treatments like physiotherapy, heart monitoring and breathing support that help patients function and feel better by avoiding complications from DMD.
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Date of preparation: September 2022
Neuromuscular disorders affect the muscles and nerves, and most of the causes are genetic. This means they are either passed down through the family or caused by changes in an individual person’s genes.
Most neuromuscular disorders cause muscle weakness that worsens over time. Signs and symptoms of neuromuscular diseases can vary and may be mild, moderate, or severe.
Most often, when a child has a neuromuscular disease, they don’t grow and develop as fast as other children their age. They are often slow to start lifting their head, sitting, walking, and talking.
Treatment and supportive care may improve the symptoms of a neuromuscular disorder, increasing mobility and even life expectancy.
Muscular dystrophy is the term for a group of neuromuscular disorders that cause muscle weakness and muscle loss.
Duchenne muscular dystrophy (DMD) is a type of muscular dystrophy that causes muscle weakness that worsens over time. The progression and symptoms can vary from person to person.